cureCADASIL held a half-day Patient-Investigator Meeting June 24 at the United Leukodystrophy Foundation (ULF) Scientific Symposium and Family Conference in Itasca, Illinois.
Below is the Patient-Investigator Meeting Program as well as a link to hear the recordings from the day.
|9:00 – 9:10||Welcome and why we are here||Bertram Kasiske, MD|
|9:10 – 9:35||“The Need for Patient Engagement in the Landscape of|
|Jane Gunther, PhD, DABT|
Science Officer, cureCADASIL
|9:35 – 10:00||“Pathways for the Identification of Potential Therapeutic Targets|
for the Treatment of CADASIL”
|Stephen Fitzsimons, PhD|
Elahi Lab, Icahn School of Medicine at Mount Sinai, NY
|10:00 – 10:25||“The CADASIL Consortium: A Multicentered Natural History Study”||Jane Paulsen, PhD|
University of Wisconsin, Madison
|10:25 – 10:50||“Unraveling CADASIL: the NIH Patient-Centered CADASIL|
Program to Understand the Mechanism and Clinical Phenotypes”
|Manfred Boehm, MD|
National Heart and Lung Blood Institute, NIH, Bethesda, MD
|10:50 – 11:15||“Notch3 Signaling and Aggregation as Targets for the Treatment|
of CADASIL and Other NOTCH3-Associated Small-Vessel Diseases”
|Joseph Arboleda-Velasquez, MD, PhD|
Harvard Medical School, Boston, MA
|11:15 – 11:30||Break|
|11:30 – 12:30||Panel Discussion with Questions and Comments from the Audience||Speakers and Audience|
Upper Left: The panelists answering questions during the panel discussion at the Patient-Investigator Meeting. Upper Middle: Jane Gunther, Fanny Elahi, and Bertram Kasiske attending the United Leukodystrophy Foundation Scientific Symposium. Upper Right: United Leukodystrophy Foundation dinner event. Lower Left: Dr. Arboleda-Velasquez presenting at the Patient-Investigator Meeting. Lower Middle: Dr. Manfred Boehm presenting at the Patient-Investigator Meeting. Lower Right: Dr. Jane Paulsen presenting at the Patient-Investigator Meeting.