cureCADASIL held a half-day Patient-Investigator Meeting June 24 at the United Leukodystrophy Foundation (ULF) Scientific Symposium and Family Conference in Itasca, Illinois.
Below is the Patient-Investigator Meeting Program as well as a link to hear the recordings from the day.
| Time | Topic | Speaker |
|---|---|---|
| 9:00 – 9:10 | Welcome and why we are here | Bertram Kasiske, MD President, cureCADASIL |
| 9:10 – 9:35 | “The Need for Patient Engagement in the Landscape of Potential Therapeutics” |
Jane Gunther, PhD, DABT Science Officer, cureCADASIL |
| 9:35 – 10:00 | “Pathways for the Identification of Potential Therapeutic Targets for the Treatment of CADASIL” |
Stephen Fitzsimons, PhD Elahi Lab, Icahn School of Medicine at Mount Sinai, NY |
| 10:00 – 10:25 | “The CADASIL Consortium: A Multicentered Natural History Study” | Jane Paulsen, PhD University of Wisconsin, Madison |
| 10:25 – 10:50 | “Unraveling CADASIL: the NIH Patient-Centered CADASIL Program to Understand the Mechanism and Clinical Phenotypes” |
Manfred Boehm, MD National Heart and Lung Blood Institute, NIH, Bethesda, MD |
| 10:50 – 11:15 | “Notch3 Signaling and Aggregation as Targets for the Treatment of CADASIL and Other NOTCH3-Associated Small-Vessel Diseases” | Joseph Arboleda-Velasquez, MD, PhD Harvard Medical School, Boston, MA |
| 11:15 – 11:30 | Break | |
| 11:30 – 12:30 | Panel Discussion with Questions and Comments from the Audience | Speakers and Audience |
To look back at the event, see the website here.
Upper Left: The panelists answering questions during the panel discussion at the Patient-Investigator Meeting. Upper Middle: Jane Gunther, Fanny Elahi, and Bertram Kasiske attending the United Leukodystrophy Foundation Scientific Symposium. Upper Right: United Leukodystrophy Foundation dinner event. Lower Left: Dr. Arboleda-Velasquez presenting at the Patient-Investigator Meeting. Lower Middle: Dr. Manfred Boehm presenting at the Patient-Investigator Meeting. Lower Right: Dr. Jane Paulsen presenting at the Patient-Investigator Meeting.
